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1
Gapmers: Methods and Protocols
Springer US;Humana
Toshifumi Yokota
,
Rika Maruyama
gapmer
rna
gapmers
antisense
doi.org
gene
oligonucleotides
nucleic
rnase
patients
lna
dna
μl
protein
target
aso
asos
mrna
clinical
oligonucleotide
levels
inotersen
dystrophy
knockdown
acids
modified
familial
binding
buffer
pcr
transfection
specific
yokota
methods
solution
rnas
targeting
therapeutic
malat1
mix
silencing
therapy
activity
mol
toshifumi
samples
volanesorsen
effects
mice
ttr
Tahun:
2020
Bahasa:
english
File:
PDF, 6.03 MB
Tag Anda:
0
/
0
english, 2020
2
Antisense Drug Technology: Principles, Strategies, and Applications, Second Edition
Stanley T. Crooke
antisense
rna
oligonucleotide
oligonucleotides
protein
aso
target
effects
asos
activity
rnase
lna
mrna
figure
sirna
qxd
dna
gene
nucleic
dose
patients
studies
mice
clinical
drugs
modified
binding
administration
delivery
levels
liver
tissue
technology
observed
phosphorothioate
specific
inhibition
modifications
splicing
synthesis
cpg
targeting
acids
plasma
therapeutic
reduction
shown
effect
generation
therapy
Tahun:
2007
Bahasa:
english
File:
PDF, 7.33 MB
Tag Anda:
0
/
0
english, 2007
3
Advances in nucleic acid therapeutics
Royal Society of Chemistry
Agrawal
,
Sudhir
,
Gait
,
Michael J
rna
published
dna
february
pubs.rsc.org
target
nucleic
asos
clinical
protein
delivery
binding
gene
oligonucleotides
therapeutic
aptamer
targeting
aso
sirna
studies
acids
2ʹ
figure
activity
antisense
hiv
specific
modifications
oligonucleotide
ther
aptamers
liver
mol
patients
rnai
therapeutics
splicing
chemistry
agrawal
mediated
repeat
sirnas
activation
modified
diseases
genome
shown
effects
receptor
tlr9
Tahun:
2019
Bahasa:
english
File:
PDF, 19.02 MB
Tag Anda:
0
/
0
english, 2019
4
Advances in Nucleic Acid Therapeutics
Royal Society of Chemistry
Sudhir Agrawal
,
Michael J. Gait
rna
published
dna
february
downloaded
pubs.rsc.org
target
technological
nanyang
nucleic
asos
clinical
protein
delivery
binding
gene
oligonucleotides
therapeutic
aptamer
targeting
aso
sirna
studies
acids
2ʹ
figure
activity
antisense
hiv
specific
modifications
oligonucleotide
ther
aptamers
liver
mol
patients
rnai
therapeutics
splicing
chemistry
agrawal
mediated
repeat
sirnas
activation
modified
diseases
genome
shown
Tahun:
2019
Bahasa:
english
File:
PDF, 19.03 MB
Tag Anda:
0
/
0
english, 2019
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